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Home > "C" Clinical Trials Conditions > Chemotherapy Plus Peripheral Stem Cell Transplantation in Treating Infants With Malignant Brain or Spinal Cord Tumors

Chemotherapy Plus Peripheral Stem Cell Transplantation in Treating Infants With Malignant Brain or Spinal Cord Tumors



Chemotherapy Plus Peripheral Stem Cell Transplantation in Treating Infants With Malignant Brain or Spinal Cord Tumors

For Condition: childhood rhabdoid tumor of the central nervous system,childhood rhabdomyosarcoma,Neuroblastoma,childhood spinal cord tumors,childhood brain tumor
Status: Recruiting
Sponsor(s): Children's Oncology Group , National Cancer Institute (NCI)
Synopsis: RATIONALE: Drugs used in chemotherapy use different ways to stop tumor cells from dividing so they stop growing or die. Combining chemotherapy with peripheral stem cell transplantation may allow the doctors to give higher doses of chemotherapy drugs and kill more tumor cells. PURPOSE: Phase I trial to study the effectiveness of combination chemotherapy plus peripheral stem cell transplantation in treating infants with malignant brain or spinal cord tumors.
Details: OBJECTIVES: - Determine the maximum tolerated dose of thiotepa in infants with malignant brain or spinal cord tumors receiving intensive chemotherapy. - Determine the feasibility and toxicity of intensive chemotherapy with peripheral blood stem cell (PBSC) rescue in these patients. - Assess the feasibility of harvesting PBSCs in these patients. - Determine the complete response rate and overall event-free survival rate in patients treated with this regimen. OUTLINE: This is a pilot, multicenter study. Patients undergo surgery for diagnosis and maximal tumor resection. Within 6 weeks of surgery or when stable, patients begin induction chemotherapy comprising cisplatin IV over 6 hours on day 0; vincristine IV on days 0, 7, and 14; cyclophosphamide IV over 1 hour on days 1-2; and etoposide IV over 1 hour on days 0-2. Twenty four hours after the last cyclophosphamide dose, patients receive filgrastim (G-CSF) subcutaneously (SC) and undergo peripheral blood stem cell harvest 2 days later. Treatment repeats every 21 days for up to 3 courses in the absence of disease progression or unacceptable toxicity. Within 6 weeks after induction chemotherapy, patients receive consolidation chemotherapy comprising carboplatin IV over 2 hours on days 0-1 followed immediately by escalating doses of thiotepa IV over 2 hours. Patients then undergo peripheral blood stem cell transplantation 48 hours after the last thiotepa dose. Patients receive G-CSF SC daily on days 3 to 21. Treatment repeats every 21 days for up to 3 courses in the absence of disease progression or unacceptable toxicity. Patients experiencing dose-limiting toxicity due to thiotepa are removed from the study. Patients are followed at 4 weeks, every 3 months for 1 year, every 6 months for 3 years, and then annually for 3 years or until relapse. PROJECTED ACCRUAL: A total of 83 patients will be accrued for this study within 1 year.
Eligibility:
Study Type:
  Interventional, Treatment
Minimum Age/Maximum Age: /2 Years
Genders: Both
Protocol Entry Criteria: DISEASE CHARACTERISTICS: - Histologically proven malignant brain or spinal cord tumor, including the following: - Primitive neuroectodermal tumor - Ganglioneuroblastoma - Medulloblastoma neuroblastoma - Desmoplastic medulloblastoma - Medulloepithelioma - Ependymoma neuroepithelioma - Anaplastic ependymoma germ cell tumor - Astrocytoma germinoma - Anaplastic astrocytoma - Embryonal carcinoma - Glioblastoma endodermal sinus tumor - Gliosarcoma malignant teratoma - Choroid plexus carcinoma - Mixed germ cell tumor - Cerebellar sarcoma - Pineoblastoma - Atypical teratoid/rhabdoid tumor - Choriocarcinoma - Teratoma (malignant or with malignant transformations) - Diffusely involved brain stem tumors allowed if there is evidence of brain stem glioma by CT scan or MRI PATIENT CHARACTERISTICS: Age: - 6 months to less than 3 years Performance Status: - Not specified Life Expectancy: - More than 8 weeks Hematopoietic: - Absolute neutrophil count greater than 1,000/mm^3 - Platelet count greater than 100,000/mm^3 Hepatic: - Bilirubin less than 2.0 mg/dL Renal: - Glomerular filtration rate or creatinine clearance greater than 70 mL/min PRIOR CONCURRENT THERAPY: Biologic therapy: - No prior biologic therapy Chemotherapy: - No prior chemotherapy Endocrine therapy: - Prior corticosteroids allowed Radiotherapy: - No prior radiotherapy Surgery: - No more than 6 weeks since prior surgery - Recovered from prior surgery (stable)
Total Enrollment: 

Location and Contact Information:

Overall Study Official:
BruceCohen,  Study Chair,  Cleveland Clinic Cancer Center

Deaconess Medical Center *Recruiting*
Spokane,  Washington,  99210-0248
United States
Recruiting Frank  Reynolds 509-473-7230

Southern Illinois University School of Medicine *Recruiting*
Springfield,  Illinois,  62794-9658
United States
Recruiting Gregory  Brandt 217-545-5817

Cincinnati Children's Hospital Medical Center *Recruiting*
Cincinnati,  Ohio,  45229-3039
United States
Recruiting John  Perentesis 513-636-6090

Schneider Children's Hospital *Recruiting*
New Hyde Park,  New York,  11042
United States
Recruiting Arlene  Redner 718-470-3460

University of Illinois Medical Center *Recruiting*
Chicago,  Illinois,  60612-7243
United States
Recruiting Helen  Johnstone 312-996-6144

Indiana University Cancer Center *Recruiting*
Indianapolis,  Indiana,  46202-5225
United States
Recruiting Robert  Fallon 317-274-8784

Chao Family Comprehensive Cancer Center at University of California Irvine Cancer Center *Recruiting*
Orange,  California,  92868
United States
Recruiting Stanley  Calderwood 714-456-6615

St. Barnabas Medical Center *Recruiting*
Livingston,  New Jersey,  07039
United States
Recruiting Brenda  Sison 973-322-2800

Sydney Children's Hospital *Recruiting*
Randwick,  New South Wales,  2031
Australia
Recruiting Glenn  Marshall 61-2-9382-1721

State University of New York Health Science Center at Brooklyn College of Medicine *Recruiting*
Brooklyn,  New York,  11203
United States
Recruiting Sreedhar  Rao 718-270-1693

Gundersen Lutheran Cancer Center at Gundersen Lutheran Medical Center *Recruiting*
La Crosse,  Wisconsin,  54601
United States
Recruiting Robert  Ettinger 608-782-7300

Phoenix Children's Hospital *Recruiting*
Phoenix,  Arizona,  85016-7710
United States
Recruiting Paul  Baranko 602-546-0920

Cardinal Bernardin Cancer Center at Loyola University Medical Center *Recruiting*
Maywood,  Illinois,  60153
United States
Recruiting Ricarchito  Manera 708-327-9136

Geisinger Medical Center *Recruiting*
Danville,  Pennsylvania,  17822-1320
United States
Recruiting Jeffrey  Taylor 570-271-6848

Rainbow Babies and Children's Hospital *Recruiting*
Cleveland,  Ohio,  44106
United States
Recruiting Eric  Kodish 216-844-3345

Palmetto Health South Carolina Cancer Center *Recruiting*
Columbia,  South Carolina,  29203
United States
Recruiting Ronnie  Neuberg 803-434-3533

Albert Einstein Clinical Cancer Center *Recruiting*
Bronx,  New York,  10461
United States
Recruiting Eva  Radel 718-920-7844

Holden Comprehensive Cancer Center at University of Iowa *Recruiting*
Iowa City,  Iowa,  52242-1009
United States
Recruiting Raymond  Tannous 319-356-1905

University of Texas - MD Anderson Cancer Center *Recruiting*
Houston,  Texas,  77030-4009
United States
Recruiting Joann  Ater 713-792-6665

UNMC Eppley Cancer Center at the University of Nebraska Medical Center *Recruiting*
Omaha,  Nebraska,  68198-2168
United States
Recruiting Peter  Coccia 402-559-7257

Loma Linda University Cancer Institute at Loma Linda University Medical Center *Recruiting*
Loma Linda,  California,  92354
United States
Recruiting Antranik  Bedros 909-558-3391

Children's Hospitals and Clinics - Minnesota *Recruiting*
St. Paul,  Minnesota,  55102
United States
Recruiting Christopher  Moertel 651-220-6732

Markey Cancer Center at University of Kentucky Chandler Medical Center *Recruiting*
Lexington,  Kentucky,  40536-0284
United States
Recruiting Martha  Greenwood 859-323-6771

Covenant Children's Hospital *Recruiting*
Lubbock,  Texas,  79410
United States
Recruiting John  Iacuone 806-725-1011

CancerCare Manitoba *Recruiting*
Winnipeg,  Manitoba,  R3E 0V9
Canada
Recruiting Rochelle  Yanofsky 204-787-4163

Cleveland Clinic Taussig Cancer Center *Recruiting*
Cleveland,  Ohio,  44195
United States
Recruiting Joanne  Hilden 216-444-8407

Sunrise Hospital and Medical Center *Recruiting*
Las Vegas,  Nevada,  89119
United States
Recruiting Paul  Kent 702-737-0017

University of Michigan Comprehensive Cancer Center *Recruiting*
Ann Arbor,  Michigan,  48109-0914
United States
Recruiting Raymond  Hutchinson 734-936-8785

St. Vincent Hospital and Health Care Center *Recruiting*
Indianapolis,  Indiana,  46260
United States
Recruiting Randy  Hock 317-338-4673

Mountain States Tumor Institute - Boise *Recruiting*
Boise,  Idaho,  83712
United States
Recruiting J.  Johnston 208-381-2782

Children's Hospital Medical Center of Akron *Recruiting*
Akron,  Ohio,  44308
United States
Recruiting Jeffrey  Hord 330-543-8580

Forum Health-Tod Childrens Hospital *Recruiting*
Youngstown,  Ohio,  44501
United States
Recruiting Ayman  Saleh 330-884-3955

University of Wisconsin Comprehensive Cancer Center *Recruiting*
Madison,  Wisconsin,  53792-6164
United States
Recruiting Yousif  Matloub 608-263-6200

Memorial Sloan-Kettering Cancer Center *Recruiting*
New York City,  New York,  10021
United States
Recruiting Peter  Steinherz 212-639-7951

Doernbecher Children's Hospital at Oregon Health & Science University *Recruiting*
Portland,  Oregon,  97239-3098
United States
Recruiting H.  Nicholson 503-494-1543

Children's Hospital Los Angeles *Recruiting*
Los Angeles,  California,  90027-0700
United States
Recruiting Paul  Gaynon 323-669-2163

Children's Hospital of Denver *Recruiting*
Denver,  Colorado,  80218-1088
United States
Recruiting Roger  Giller 303-861-6892

Maimonides Medical Center *Recruiting*
Brooklyn,  New York,  11219
United States
Recruiting Ludovico  Guarini 718-283-8173

British Columbia Children's Hospital *Recruiting*
Vancouver,  British Columbia,  V6H 3V4
Canada
Recruiting Paul  Rogers 604-875-2322

Curtis & Elizabeth Anderson Cancer Institute at Memorial Health University Medical Center *Recruiting*
Savannah,  Georgia,  31403-3089
United States
Recruiting Ihsan  Al-Khalil 912-350-3090

Medical Center of Central Georgia *Recruiting*
Macon,  Georgia,  31201
United States
Recruiting Hassan  Dannawi 478-633-1104

Mayo Clinic Cancer Center *Recruiting*
Rochester,  Minnesota,  55905
United States
Recruiting Carola  Arndt 507-284-2511

Meritcare Roger Maris Cancer Center *Recruiting*
Fargo,  North Dakota,  58122
United States
Recruiting Nathan  Kobrinsky 701-234-7544

Presbyterian-St Luke's Medical Center *Recruiting*
Denver,  Colorado,  80218
United States
Recruiting Patsy  Cullen 303-832-2462

St. Joseph's Hospital and Medical Center *Recruiting*
Paterson,  New Jersey,  07503
United States
Recruiting Mary  Bonilla 973-754-3230

Kosair Children's Hospital *Recruiting*
Louisville,  Kentucky,  40202-3830
United States
Recruiting Salvatore  Bertolone 502-852-8450

City of Hope Comprehensive Cancer Center *Recruiting*
Duarte,  California,  91010-3000
United States
Recruiting Judith  Sato 626-930-5430

Cancer Institute of New Jersey *Recruiting*
New Brunswick,  New Jersey,  08903
United States
Recruiting Richard  Drachtman 732-235-7898

Kaiser Permanente Medical Center - San Francisco Geary Campus *Recruiting*
San Francisco,  California,  94115
United States
Recruiting Kenneth  Leung 415-833-3528

Penn State Cancer Institute at Milton S. Hershey Medical Center *Recruiting*
Hershey,  Pennsylvania,  17033-0850
United States
Recruiting John  Neely 717-531-6012

Alfred I. duPont Hospital for Children *Recruiting*
Wilmington,  Delaware,  19899
United States
Recruiting Gregory  Griffin 302-651-5500

Children's Hospitals and Clinics - Minneapolis *Recruiting*
Minneapolis,  Minnesota,  55404
United States
Recruiting Maura  O'Leary 612-813-5940

Sinai Hospital of Baltimore *Recruiting*
Baltimore,  Maryland,  21225
United States
Recruiting Joseph  Wiley 410-601-5864

Josephine Ford Cancer Center at Henry Ford Hospital *Recruiting*
Detroit,  Michigan,  48202
United States
Recruiting Hassan  Yaish 313-916-3138

Princess Margaret Hospital for Children *Recruiting*
Perth,  Western Australia,  6006
Australia
Recruiting Marianne  Phillips 61-8-9340-8222

Newark Beth Israel Medical Center *Recruiting*
Newark,  New Jersey,  07112-2094
United States
Recruiting Peri  Kamalakar 973-926-7161

Herbert Irving Comprehensive Cancer Center at Columbia University *Recruiting*
New York City,  New York,  10032
United States
Recruiting Linda  Granowetter 212-305-8652

Children's Hospital Central California *Recruiting*
Madera,  California,  93638-8762
United States
Recruiting Vonda  Crouse 559-353-5480

Children's National Medical Center *Recruiting*
Washington D.C.,  District of Columbia,  20010-2970
United States
Recruiting Nita  Seibel 202-884-2144

Children's Hospital and Regional Medical Center - Seattle *Recruiting*
Seattle,  Washington,  98105
United States
Recruiting J.  Geyer 206-987-6664

Children's Hospital of Orange County *Recruiting*
Orange,  California,  92868
United States
Recruiting Wei-Ping  Shen 714-532-8636

Children's Hospital of Austin *Recruiting*
Austin,  Texas,  78701
United States
Recruiting Sharon  Lockhart 512-324-8480

Children's Hospital of the King's Daughters *Recruiting*
Norfolk,  Virginia,  23507
United States
Recruiting Rebecca  Byrd 757-668-7243

Janeway Children's Health and Rehabilitation Centre *Recruiting*
St. John's,  Newfoundland and Labrador,  A1B 3V6
Canada
Recruiting John  Hand 709-777-4799

Brooklyn Hospital Center *Recruiting*
Brooklyn,  New York,  11201-5493
United States
Recruiting Swayamprabha  Sadanandan 718-250-6074

Children's Hospital of Philadelphia *Recruiting*
Philadelphia,  Pennsylvania,  19104
United States
Recruiting Beverly  Lange 215-590-2249

William Beaumont Hospital - Royal Oak *Recruiting*
Royal Oak,  Michigan,  48073-6769
United States
Recruiting Charles  Main 248-551-0360

Children's Mercy Hospital *Recruiting*
Kansas City,  Missouri,  64108
United States
Recruiting Maxine  Hetherington 816-234-3265

Primary Children's Medical Center *Recruiting*
Salt Lake City,  Utah,  84113
United States
Recruiting Carol  Bruggers 801-588-2680

New York Weill Cornell Cancer Center at Cornell University *Recruiting*
New York City,  New York,  10021
United States
Recruiting Patricia  Giardina 212-746-3400

Valerie Fund Children's Center at Atlantic Health *Recruiting*
Summit,  New Jersey,  07901
United States
Recruiting Hazem  Mahmoud 973-971-6731

NYU School of Medicine's Kaplan Comprehensive Cancer Center *Recruiting*
New York City,  New York,  10016
United States
Recruiting Aaron  Rausen 212-263-7144

David Grant Medical Center *Recruiting*
Travis Air Force Base,  California,  94535
United States
Recruiting Peter  Chenaille 707-423-7176

UCSF Comprehensive Cancer Center *Recruiting*
San Francisco,  California,  94115
United States
Recruiting Katherine  Matthay 415-353-9510

Santa Barbara Cottage Hospital *Recruiting*
Santa Barbara,  California,  93102
United States
Recruiting Felicity  Hodder 805-569-8394

New York Medical College *Recruiting*
Valhalla,  New York,  10595
United States
Recruiting M.  Ozkaynak 914-493-7997

University of Connecticut Cancer Center at University of Connecticut Health Center *Recruiting*
Farmington,  Connecticut,  06360-7106
United States
Recruiting Arnold  Altman 860-545-9630

Lombardi Cancer Center at Georgetown University Medical Center *Recruiting*
Washington D.C.,  District of Columbia,  20007
United States
Recruiting Aziza  Shad 202-687-2224

Cabell Huntington Hospital *Recruiting*
Huntington,  West Virginia,  25701
United States
Recruiting Andrew  Pendleton 304-691-1384

Children's Hospital of Pittsburgh *Recruiting*
Pittsburgh,  Pennsylvania,  15213
United States
Recruiting Arthur  Ritchey 412-692-5949

Children's Hospital of Omaha *Recruiting*
Omaha,  Nebraska,  68114
United States
Recruiting Minnie  Abromowitch 402-955-3950

Mary Bridge Children's Health Center *Recruiting*
Tacoma,  Washington,  98415-0299
United States
Recruiting William  Thomas 253-403-4915

Baystate Medical Center *Recruiting*
Springfield,  Massachusetts,  01107
United States
Recruiting David  Steele 413-794-9338

Texas Tech University Health Sciences Center School of Medicine *Recruiting*
Amarillo,  Texas,  79106
United States
Recruiting Osvaldo  Regueira 806-354-5706

Vanderbilt-Ingram Cancer Center at Vanderbilt Medical Center *Recruiting*
Nashville,  Tennessee,  37232-6838
United States
Recruiting James  Whitlock 615-936-1762

Jonathan Jaques Children's Cancer Center at Miller Children's Hospital *Recruiting*
Long Beach,  California,  90801-1428
United States
Recruiting William  Roberts 562-933-8600

Raymond Blank Memorial Hospital for Children *Recruiting*
Des Moines,  Iowa,  50308
United States
Recruiting Torrey  Mitchell 515-241-8912

Bellin Memorial Hospital *Recruiting*
Green Bay,  Wisconsin,  54301
United States
Recruiting Dorothy  Ganick 920-433-6025

Children's Hospital of Columbus *Recruiting*
Columbus,  Ohio,  43205-2696
United States
Recruiting Frederick  Ruymann 614-722-3564

Lineberger Comprehensive Cancer Center at University of North Carolina - Chapel Hill *Recruiting*
Chapel Hill,  North Carolina,  27599-7295
United States
Recruiting Stuart  Gold 919-966-0985

University of Minnesota Cancer Center *Recruiting*
Minneapolis,  Minnesota,  55455
United States
Recruiting Joseph  Neglia 612-626-2778

Toledo Children's Hospital *Recruiting*
Toledo,  Ohio,  43601
United States
Recruiting Richard  Shore 419-471-5437

Methodist Cancer Center at Methodist Specialty and Transplant Hospital *Recruiting*
San Antonio,  Texas,  78229-3902
United States
Recruiting Jaime  Estrada 210-575-8130

Allan Blair Cancer Centre *Recruiting*
Regina,  Saskatchewan,  S4T 7T1
Canada
Recruiting Christina  Suan Goh 306-766-2205

St. Vincent Mercy Medical Center *Recruiting*
Toledo,  Ohio,  43608
United States
Recruiting Rama  Jasty 419-251-8215

Starship Children's Hospital *Recruiting*
Auckland,  , 
New Zealand
Recruiting Lochie  Teague 64-9-307-4949 ext. 6295

Southern California Permanente Medical Group *Recruiting*
Downey,  California,  90242
United States
Recruiting Willye  Powell 562-803-2472

Avera Cancer Institute *Recruiting*
Sioux Falls,  South Dakota,  57105-1080
United States
Recruiting Marwan  Hanna 605-322-7595

Cedars-Sinai Comprehensive Cancer Center at Cedars-Sinai Medical Center *Recruiting*
Los Angeles,  California,  90048
United States
Recruiting Carole  Hurvitz 310-423-4423

Brookdale University Hospital and Medical Center *Recruiting*
Brooklyn,  New York,  11212
United States
Recruiting Kusum  Viswanathan 718-240-5904

Lutheran General Cancer Care Center *Recruiting*
Park Ridge,  Illinois,  60068-1174
United States
Recruiting Jong-Hyo  Kwon 847-723-5962

Sioux Valley Hospital at University of South Dakota Medical Center *Recruiting*
Sioux Falls,  South Dakota,  57117
United States
Recruiting Jakica  Tancabelic 605-333-7171

CCOP - Duluth *Recruiting*
Duluth,  Minnesota,  55805
United States
Recruiting Robert  Niedringhaus 218-786-8364

East Tennessee Children's Hospital *Recruiting*
Knoxville,  Tennessee,  37901
United States
Recruiting Ray  Pais 865-541-8266

Dakota Cancer Institute at Innovis Health - Dakota Clinic *Recruiting*
Fargo,  North Dakota,  58103-4940
United States
Recruiting Janet  Tillisch 701-364-4966

Group Health Eastside Hospital *Recruiting*
Redmond,  Washington,  98052
United States
Recruiting Philip  Herzog 206-883-5840

Children's Hospital of Western Ontario *Recruiting*
London,  Ontario,  N6C 2V5
Canada
Recruiting Anne  Lois Cairney 519-685-8494

Spectrum Health and DeVos Children's Hospital *Recruiting*
Grand Rapids,  Michigan,  49503
United States
Recruiting David  Freyer 616-391-2086

Children's Medical Center *Recruiting*
Augusta,  Georgia,  30912-3730
United States
Recruiting Roger  Vega 706-721-3626

University of Chicago Cancer Research Center *Recruiting*
Chicago,  Illinois,  60601
United States
Recruiting James  Nachman 773-702-6808

CCOP - Kalamazoo *Recruiting*
Kalamazoo,  Michigan,  49007-3731
United States
Recruiting Leonard  Mattano 269-373-7450

Jonsson Comprehensive Cancer Center, UCLA *Recruiting*
Los Angeles,  California,  90095-1781
United States
Recruiting Stephen  Feig 310-825-5268

Children's Hospital and Research Center at Oakland *Recruiting*
Oakland,  California,  94609-1809
United States
Recruiting James  Feusner 510-428-3000

Children's Medical Center - Dayton *Recruiting*
Dayton,  Ohio,  45404
United States
Recruiting Emmett  Broxson 937-641-3111


Additional Information:
Study ID Numbers:
  CDR0000065924;  COG-99703,CCG-99703
Study Start Date: 
Record last reviewed: May 2004
Additional information available at: clinicaltrials.gov
Clinicaltrials.gov Reference link: NCT00003141

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2. Chemotherapy and Radiation Therapy After Surgery in Treating Children With Newly Diagnosed Astrocytoma, Glioblastoma Multiforme, or Gliosarcoma

3. Cilengitide in Treating Children With Refractory Primary Brain Tumors

4. Temozolomide and O6-Benzylguanine in Treating Children With Recurrent Brain Tumors

5. Carboplatin, Vincristine, and Temozolomide in Treating Children With Progressive and/or Symptomatic Low-Grade Glioma

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